Pompe Disease Treatment Market by Treatment (Enzyme Replacement Therapy (ERT), Substrate Reduction Therapy (SRT), Chaperone-Advanced Replacement Therapy (CART), and Others), Route of Administration (Oral, Intravenous, and Others), Distribution Channel (Hospital and Clinics Pharmacies, Retail Pharmacies, Online Pharmacies, and Others), Indication Type (Infantile-Onset Pompe Disease (IOPD), Classic Infantile Form, Non-Classic Infantile Form, Late-Onset Pompe Disease (LOPD), and Others), and Region 2025-2033

Pompe Disease Treatment Market by Treatment (Enzyme Replacement Therapy (ERT), Substrate Reduction Therapy (SRT), Chaperone-Advanced Replacement Therapy (CART), and Others), Route of Administration (Oral, Intravenous, and Others), Distribution Channel (Hospital and Clinics Pharmacies, Retail Pharmacies, Online Pharmacies, and Others), Indication Type (Infantile-Onset Pompe Disease (IOPD), Classic Infantile Form, Non-Classic Infantile Form, Late-Onset Pompe Disease (LOPD), and Others), and Region 2025-2033

Report Format: PDF+Excel | Report ID: SR112025A6708

1    Preface
2    Scope and Methodology

    2.1    Objectives of the Study
    2.2    Stakeholders
    2.3    Data Sources
        2.3.1    Primary Sources
        2.3.2    Secondary Sources
    2.4    Market Estimation
        2.4.1    Bottom-Up Approach
        2.4.2    Top-Down Approach
    2.5    Forecasting Methodology
3    Executive Summary
4    Introduction

    4.1    Overview
    4.2    Key Industry Trends
5    Global Pompe Disease Treatment Market
    5.1    Market Overview
    5.2    Market Performance
    5.3    Impact of COVID-19
    5.4    Market Forecast
6    Market Breakup by Treatment
    6.1    Enzyme Replacement Therapy (ERT)
        6.1.1 Market Trends
        6.1.2 Market Forecast
    6.2    Substrate Reduction Therapy (SRT)
        6.2.1 Market Trends
        6.2.2 Market Forecast
    6.3    Chaperone-Advanced Replacement Therapy (CART)
        6.3.1 Market Trends
        6.3.2 Market Forecast
    6.4    Others
        6.4.1 Market Trends
        6.4.2 Market Forecast
7    Market Breakup by Route of Administration
    7.1    Oral
        7.1.1 Market Trends
        7.1.2 Market Forecast
    7.2    Intravenous
        7.2.1 Market Trends
        7.2.2 Market Forecast
    7.3    Others
        7.3.1 Market Trends
        7.3.2 Market Forecast
8    Market Breakup by Distribution Channel
    8.1    Hospital & Clinics Pharmacies 
        8.1.1 Market Trends
        8.1.2 Market Forecast
    8.2    Retail Pharmacies 
        8.2.1 Market Trends
        8.2.2 Market Forecast
    8.3    Online Pharmacies 
        8.3.1 Market Trends
        8.3.2 Market Forecast
    8.4    Others
        8.4.1 Market Trends
        8.4.2 Market Forecast
9    Market Breakup by Indication Type
    9.1    Infantile-Onset Pompe Disease (IOPD)
        9.1.1 Market Trends
        9.1.2 Market Forecast
    9.2    Classic Infantile Form
        9.2.1 Market Trends
        9.2.2 Market Forecast
    9.3    Non-Classic Infantile Form
        9.3.1 Market Trends
        9.3.2 Market Forecast
    9.4    Late-Onset Pompe Disease (LOPD)
        9.4.1 Market Trends
        9.4.2 Market Forecast
    9.5    Others
        9.5.1 Market Trends
        9.5.2 Market Forecast
10    Market Breakup by Region
    10.1    North America
        10.1.1 United States
           10.1.1.1 Market Trends
           10.1.1.2 Market Forecast
        10.1.2 Canada
           10.1.2.1 Market Trends
           10.1.2.2 Market Forecast
    10.2    Asia-Pacific
        10.2.1 China
           10.2.1.1 Market Trends
           10.2.1.2 Market Forecast
        10.2.2 Japan
           10.2.2.1 Market Trends
           10.2.2.2 Market Forecast
        10.2.3 India
           10.2.3.1 Market Trends
           10.2.3.2 Market Forecast
        10.2.4 South Korea
           10.2.4.1 Market Trends
           10.2.4.2 Market Forecast
        10.2.5 Australia
           10.2.5.1 Market Trends
           10.2.5.2 Market Forecast
        10.2.6 Indonesia
           10.2.6.1 Market Trends
           10.2.6.2 Market Forecast
        10.2.7 Others
           10.2.7.1 Market Trends
           10.2.7.2 Market Forecast
    10.3    Europe
        10.3.1 Germany
           10.3.1.1 Market Trends
           10.3.1.2 Market Forecast
        10.3.2 France
           10.3.2.1 Market Trends
           10.3.2.2 Market Forecast
        10.3.3 United Kingdom
           10.3.3.1 Market Trends
           10.3.3.2 Market Forecast
        10.3.4 Italy
           10.3.4.1 Market Trends
           10.3.4.2 Market Forecast
        10.3.5 Spain
           10.3.5.1 Market Trends
           10.3.5.2 Market Forecast
        10.3.6 Russia
           10.3.6.1 Market Trends
           10.3.6.2 Market Forecast
        10.3.7 Others
           10.3.7.1 Market Trends
           10.3.7.2 Market Forecast
    10.4    Latin America
        10.4.1 Brazil
           10.4.1.1 Market Trends
           10.4.1.2 Market Forecast
        10.4.2 Mexico
           10.4.2.1 Market Trends
           10.4.2.2 Market Forecast
        10.4.3 Others
           10.4.3.1 Market Trends
           10.4.3.2 Market Forecast
    10.5    Middle East and Africa
        10.5.1 Market Trends
        10.5.2 Market Breakup by Country
        10.5.3 Market Forecast
11    Drivers, Restraints, and Opportunities
    11.1    Overview
    11.2    Drivers
    11.3    Restraints
    11.4    Opportunities
12    Value Chain Analysis
13    Porters Five Forces Analysis

    13.1    Overview
    13.2    Bargaining Power of Buyers
    13.3    Bargaining Power of Suppliers
    13.4    Degree of Competition
    13.5    Threat of New Entrants
    13.6    Threat of Substitutes
14    Price Analysis
15    Competitive Landscape

    15.1    Market Structure
    15.2    Key Players
    15.3    Profiles of Key Players
        15.3.1    Amicus Therapeutics Inc.
           15.3.1.1 Company Overview
           15.3.1.2 Product Portfolio
           15.3.1.3 Financials
           15.3.1.4 SWOT Analysis
        15.3.2    Audentes Therapeutics Inc. (Astellas US Holding Inc.)
           15.3.2.1 Company Overview
           15.3.2.2 Product Portfolio
        15.3.3    Oxyrane UK Limited
           15.3.3.1 Company Overview
           15.3.3.2 Product Portfolio
        15.3.4    Sanofi S.A.
           15.3.4.1 Company Overview
           15.3.4.2 Product Portfolio
           15.3.4.3 Financials
           15.3.4.4 SWOT Analysis
        15.3.5    Spark Therapeutics Inc.
           15.3.5.1 Company Overview
           15.3.5.2 Product Portfolio

Kindly, note that this only represents a partial list of companies, and the complete list has been provided in the report

List of Figures

​Figure 1: Global: Pompe Disease Treatment Market: Major Drivers and Challenges
Figure 2: Global: Pompe Disease Treatment Market: Sales Value (in Billion USD), 2019-2024
Figure 3: Global: Pompe Disease Treatment Market Forecast: Sales Value (in Billion USD), 2025-2033
Figure 4: Global: Pompe Disease Treatment Market: Breakup by Treatment (in %), 2024
Figure 5: Global: Pompe Disease Treatment Market: Breakup by Route of Administration (in %), 2024
Figure 6: Global: Pompe Disease Treatment Market: Breakup by Distribution Channel (in %), 2024
Figure 7: Global: Pompe Disease Treatment Market: Breakup by Indication Type (in %), 2024
Figure 8: Global: Pompe Disease Treatment Market: Breakup by Region (in %), 2024
Figure 9: Global: Pompe Disease Treatment (Enzyme Replacement Therapy (ERT)) Market: Sales Value (in Million USD), 2019 & 2024
Figure 10: Global: Pompe Disease Treatment (Enzyme Replacement Therapy (ERT)) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 11: Global: Pompe Disease Treatment (Substrate Reduction Therapy (SRT)) Market: Sales Value (in Million USD), 2019 & 2024
Figure 12: Global: Pompe Disease Treatment (Substrate Reduction Therapy (SRT)) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 13: Global: Pompe Disease Treatment (Chaperone-Advanced Replacement Therapy (CART)) Market: Sales Value (in Million USD), 2019 & 2024
Figure 14: Global: Pompe Disease Treatment (Chaperone-Advanced Replacement Therapy (CART)) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 15: Global: Pompe Disease Treatment (Other Treatments) Market: Sales Value (in Million USD), 2019 & 2024
Figure 16: Global: Pompe Disease Treatment (Other Treatments) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 17: Global: Pompe Disease Treatment (Oral) Market: Sales Value (in Million USD), 2019 & 2024
Figure 18: Global: Pompe Disease Treatment (Oral) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 19: Global: Pompe Disease Treatment (Intravenous) Market: Sales Value (in Million USD), 2019 & 2024
Figure 20: Global: Pompe Disease Treatment (Intravenous) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 21: Global: Pompe Disease Treatment (Other Rout of Administrations) Market: Sales Value (in Million USD), 2019 & 2024
Figure 22: Global: Pompe Disease Treatment (Other Rout of Administrations) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 23: Global: Pompe Disease Treatment (Hospital & Clinics Pharmacies) Market: Sales Value (in Million USD), 2019 & 2024
Figure 24: Global: Pompe Disease Treatment (Hospital & Clinics Pharmacies) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 25: Global: Pompe Disease Treatment (Retail Pharmacies) Market: Sales Value (in Million USD), 2019 & 2024
Figure 26: Global: Pompe Disease Treatment (Retail Pharmacies) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 27: Global: Pompe Disease Treatment (Online Pharmacies) Market: Sales Value (in Million USD), 2019 & 2024
Figure 28: Global: Pompe Disease Treatment (Online Pharmacies) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 29: Global: Pompe Disease Treatment (Other Distribution Channels) Market: Sales Value (in Million USD), 2019 & 2024
Figure 30: Global: Pompe Disease Treatment (Other Distribution Channels) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 31: Global: Pompe Disease Treatment (Infantile-Onset Pompe Disease (IOPD)) Market: Sales Value (in Million USD), 2019 & 2024
Figure 32: Global: Pompe Disease Treatment (Infantile-Onset Pompe Disease (IOPD)) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 33: Global: Pompe Disease Treatment (Classic Infantile Form) Market: Sales Value (in Million USD), 2019 & 2024
Figure 34: Global: Pompe Disease Treatment (Classic Infantile Form) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 35: Global: Pompe Disease Treatment (Non-Classic Infantile Form) Market: Sales Value (in Million USD), 2019 & 2024
Figure 36: Global: Pompe Disease Treatment (Non-Classic Infantile Form) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 37: Global: Pompe Disease Treatment (Late-Onset Pompe Disease (LOPD)) Market: Sales Value (in Million USD), 2019 & 2024
Figure 38: Global: Pompe Disease Treatment (Late-Onset Pompe Disease (LOPD)) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 39: Global: Pompe Disease Treatment (Other Indication Types) Market: Sales Value (in Million USD), 2019 & 2024
Figure 40: Global: Pompe Disease Treatment (Other Indication Types) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 41: North America: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 42: North America: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 43: United States: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 44: United States: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 45: Canada: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 46: Canada: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 47: Asia-Pacific: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 48: Asia-Pacific: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 49: China: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 50: China: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 51: Japan: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 52: Japan: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 53: India: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 54: India: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 55: South Korea: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 56: South Korea: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 57: Australia: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 58: Australia: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 59: Indonesia: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 60: Indonesia: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 61: Others: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 62: Others: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 63: Europe: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 64: Europe: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 65: Germany: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 66: Germany: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 67: France: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 68: France: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 69: United Kingdom: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 70: United Kingdom: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 71: Italy: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 72: Italy: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 73: Spain: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 74: Spain: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 75: Russia: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 76: Russia: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 77: Others: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 78: Others: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 79: Latin America: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 80: Latin America: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 81: Brazil: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 82: Brazil: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 83: Mexico: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 84: Mexico: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 85: Others: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 86: Others: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 87: Middle East and Africa: Pompe Disease Treatment Market: Sales Value (in Million USD), 2019 & 2024
Figure 88: Middle East and Africa: Pompe Disease Treatment Market: Breakup by Country (in %), 2024
Figure 89: Middle East and Africa: Pompe Disease Treatment Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 90: Global: Pompe Disease Treatment Industry: Drivers, Restraints, and Opportunities
Figure 91: Global: Pompe Disease Treatment Industry: Value Chain Analysis
Figure 92: Global: Pompe Disease Treatment Industry: Porter's Five Forces Analysis

List of Tables

Table 1: Global: Pompe Disease Treatment Market: Key Industry Highlights, 2024 & 2033
Table 2: Global: Pompe Disease Treatment Market Forecast: Breakup by Treatment (in Million USD), 2025-2033
Table 3: Global: Pompe Disease Treatment Market Forecast: Breakup by Route of Administration (in Million USD), 2025-2033
Table 4: Global: Pompe Disease Treatment Market Forecast: Breakup by Distribution Channel (in Million USD), 2025-2033
Table 5: Global: Pompe Disease Treatment Market Forecast: Breakup by Indication Type (in Million USD), 2025-2033
Table 6: Global: Pompe Disease Treatment Market Forecast: Breakup by Region (in Million USD), 2025-2033
Table 7: Global: Pompe Disease Treatment Market: Competitive Structure
Table 8: Global: Pompe Disease Treatment Market: Key Players

Pompe Disease Treatment Market by Treatment (Enzyme Replacement Therapy (ERT), Substrate Reduction Therapy (SRT), Chaperone-Advanced Replacement Therapy (CART), and Others), Route of Administration (Oral, Intravenous, and Others), Distribution Channel (Hospital and Clinics Pharmacies, Retail Pharmacies, Online Pharmacies, and Others), Indication Type (Infantile-Onset Pompe Disease (IOPD), Classic Infantile Form, Non-Classic Infantile Form, Late-Onset Pompe Disease (LOPD), and Others), and Region 2025-2033
Purchase Options Discount
Offer
Benefits of Customization
  • Personalize this research
  • Triangulate with your data
  • Get data as per your format and definition
  • Gain a deeper dive into a specific application, geography, customer, or competitor
  • Any level of personalization

Get in Touch With Us

UNITED STATES

Phone: +1-631-791-1145

INDIA

Phone: +91-120-433-0800

UNITED KINGDOM

Phone: +44-753-714-6104

Email: sales@imarcgroup.com

Client Testimonials