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Pompe Disease Treatment Market by Treatment (Enzyme Replacement Therapy (ERT), Substrate Reduction Therapy (SRT), Chaperone-Advanced Replacement Therapy (CART), and Others), Route of Administration (Oral, Intravenous, and Others), Distribution Channel (Hospital and Clinics Pharmacies, Retail Pharmacies, Online Pharmacies, and Others), Indication Type (Infantile-Onset Pompe Disease (IOPD), Classic Infantile Form, Non-Classic Infantile Form, Late-Onset Pompe Disease (LOPD), and Others), and Region 2024-2032
Report Format: PDF+Excel | Report ID: SR112024A6708
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1 Preface
2 Scope and Methodology
2.1 Objectives of the Study
2.2 Stakeholders
2.3 Data Sources
2.3.1 Primary Sources
2.3.2 Secondary Sources
2.4 Market Estimation
2.4.1 Bottom-Up Approach
2.4.2 Top-Down Approach
2.5 Forecasting Methodology
3 Executive Summary
4 Introduction
4.1 Overview
4.2 Key Industry Trends
5 Global Pompe Disease Treatment Market
5.1 Market Overview
5.2 Market Performance
5.3 Impact of COVID-19
5.4 Market Forecast
6 Market Breakup by Treatment
6.1 Enzyme Replacement Therapy (ERT)
6.1.1 Market Trends
6.1.2 Market Forecast
6.2 Substrate Reduction Therapy (SRT)
6.2.1 Market Trends
6.2.2 Market Forecast
6.3 Chaperone-Advanced Replacement Therapy (CART)
6.3.1 Market Trends
6.3.2 Market Forecast
6.4 Others
6.4.1 Market Trends
6.4.2 Market Forecast
7 Market Breakup by Route of Administration
7.1 Oral
7.1.1 Market Trends
7.1.2 Market Forecast
7.2 Intravenous
7.2.1 Market Trends
7.2.2 Market Forecast
7.3 Others
7.3.1 Market Trends
7.3.2 Market Forecast
8 Market Breakup by Distribution Channel
8.1 Hospital & Clinics Pharmacies
8.1.1 Market Trends
8.1.2 Market Forecast
8.2 Retail Pharmacies
8.2.1 Market Trends
8.2.2 Market Forecast
8.3 Online Pharmacies
8.3.1 Market Trends
8.3.2 Market Forecast
8.4 Others
8.4.1 Market Trends
8.4.2 Market Forecast
9 Market Breakup by Indication Type
9.1 Infantile-Onset Pompe Disease (IOPD)
9.1.1 Market Trends
9.1.2 Market Forecast
9.2 Classic Infantile Form
9.2.1 Market Trends
9.2.2 Market Forecast
9.3 Non-Classic Infantile Form
9.3.1 Market Trends
9.3.2 Market Forecast
9.4 Late-Onset Pompe Disease (LOPD)
9.4.1 Market Trends
9.4.2 Market Forecast
9.5 Others
9.5.1 Market Trends
9.5.2 Market Forecast
10 Market Breakup by Region
10.1 North America
10.1.1 United States
10.1.1.1 Market Trends
10.1.1.2 Market Forecast
10.1.2 Canada
10.1.2.1 Market Trends
10.1.2.2 Market Forecast
10.2 Asia-Pacific
10.2.1 China
10.2.1.1 Market Trends
10.2.1.2 Market Forecast
10.2.2 Japan
10.2.2.1 Market Trends
10.2.2.2 Market Forecast
10.2.3 India
10.2.3.1 Market Trends
10.2.3.2 Market Forecast
10.2.4 South Korea
10.2.4.1 Market Trends
10.2.4.2 Market Forecast
10.2.5 Australia
10.2.5.1 Market Trends
10.2.5.2 Market Forecast
10.2.6 Indonesia
10.2.6.1 Market Trends
10.2.6.2 Market Forecast
10.2.7 Others
10.2.7.1 Market Trends
10.2.7.2 Market Forecast
10.3 Europe
10.3.1 Germany
10.3.1.1 Market Trends
10.3.1.2 Market Forecast
10.3.2 France
10.3.2.1 Market Trends
10.3.2.2 Market Forecast
10.3.3 United Kingdom
10.3.3.1 Market Trends
10.3.3.2 Market Forecast
10.3.4 Italy
10.3.4.1 Market Trends
10.3.4.2 Market Forecast
10.3.5 Spain
10.3.5.1 Market Trends
10.3.5.2 Market Forecast
10.3.6 Russia
10.3.6.1 Market Trends
10.3.6.2 Market Forecast
10.3.7 Others
10.3.7.1 Market Trends
10.3.7.2 Market Forecast
10.4 Latin America
10.4.1 Brazil
10.4.1.1 Market Trends
10.4.1.2 Market Forecast
10.4.2 Mexico
10.4.2.1 Market Trends
10.4.2.2 Market Forecast
10.4.3 Others
10.4.3.1 Market Trends
10.4.3.2 Market Forecast
10.5 Middle East and Africa
10.5.1 Market Trends
10.5.2 Market Breakup by Country
10.5.3 Market Forecast
11 Drivers, Restraints, and Opportunities
11.1 Overview
11.2 Drivers
11.3 Restraints
11.4 Opportunities
12 Value Chain Analysis
13 Porters Five Forces Analysis
13.1 Overview
13.2 Bargaining Power of Buyers
13.3 Bargaining Power of Suppliers
13.4 Degree of Competition
13.5 Threat of New Entrants
13.6 Threat of Substitutes
14 Price Analysis
15 Competitive Landscape
15.1 Market Structure
15.2 Key Players
15.3 Profiles of Key Players
15.3.1 Amicus Therapeutics Inc.
15.3.1.1 Company Overview
15.3.1.2 Product Portfolio
15.3.1.3 Financials
15.3.1.4 SWOT Analysis
15.3.2 Audentes Therapeutics Inc. (Astellas US Holding Inc.)
15.3.2.1 Company Overview
15.3.2.2 Product Portfolio
15.3.3 Oxyrane UK Limited
15.3.3.1 Company Overview
15.3.3.2 Product Portfolio
15.3.4 Sanofi S.A.
15.3.4.1 Company Overview
15.3.4.2 Product Portfolio
15.3.4.3 Financials
15.3.4.4 SWOT Analysis
15.3.5 Spark Therapeutics Inc.
15.3.5.1 Company Overview
15.3.5.2 Product Portfolio
Kindly, note that this only represents a partial list of companies, and the complete list has been provided in the report
List of Figures
Figure 1: Global: Pompe Disease Treatment Market: Major Drivers and Challenges
Figure 2: Global: Pompe Disease Treatment Market: Sales Value (in Billion US$), 2018-2023
Figure 3: Global: Pompe Disease Treatment Market Forecast: Sales Value (in Billion US$), 2024-2032
Figure 4: Global: Pompe Disease Treatment Market: Breakup by Treatment (in %), 2023
Figure 5: Global: Pompe Disease Treatment Market: Breakup by Route of Administration (in %), 2023
Figure 6: Global: Pompe Disease Treatment Market: Breakup by Distribution Channel (in %), 2023
Figure 7: Global: Pompe Disease Treatment Market: Breakup by Indication Type (in %), 2023
Figure 8: Global: Pompe Disease Treatment Market: Breakup by Region (in %), 2023
Figure 9: Global: Pompe Disease Treatment (Enzyme Replacement Therapy (ERT)) Market: Sales Value (in Million US$), 2018 & 2023
Figure 10: Global: Pompe Disease Treatment (Enzyme Replacement Therapy (ERT)) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 11: Global: Pompe Disease Treatment (Substrate Reduction Therapy (SRT)) Market: Sales Value (in Million US$), 2018 & 2023
Figure 12: Global: Pompe Disease Treatment (Substrate Reduction Therapy (SRT)) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 13: Global: Pompe Disease Treatment (Chaperone-Advanced Replacement Therapy (CART)) Market: Sales Value (in Million US$), 2018 & 2023
Figure 14: Global: Pompe Disease Treatment (Chaperone-Advanced Replacement Therapy (CART)) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 15: Global: Pompe Disease Treatment (Other Treatments) Market: Sales Value (in Million US$), 2018 & 2023
Figure 16: Global: Pompe Disease Treatment (Other Treatments) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 17: Global: Pompe Disease Treatment (Oral) Market: Sales Value (in Million US$), 2018 & 2023
Figure 18: Global: Pompe Disease Treatment (Oral) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 19: Global: Pompe Disease Treatment (Intravenous) Market: Sales Value (in Million US$), 2018 & 2023
Figure 20: Global: Pompe Disease Treatment (Intravenous) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 21: Global: Pompe Disease Treatment (Other Rout of Administrations) Market: Sales Value (in Million US$), 2018 & 2023
Figure 22: Global: Pompe Disease Treatment (Other Rout of Administrations) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 23: Global: Pompe Disease Treatment (Hospital & Clinics Pharmacies) Market: Sales Value (in Million US$), 2018 & 2023
Figure 24: Global: Pompe Disease Treatment (Hospital & Clinics Pharmacies) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 25: Global: Pompe Disease Treatment (Retail Pharmacies) Market: Sales Value (in Million US$), 2018 & 2023
Figure 26: Global: Pompe Disease Treatment (Retail Pharmacies) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 27: Global: Pompe Disease Treatment (Online Pharmacies) Market: Sales Value (in Million US$), 2018 & 2023
Figure 28: Global: Pompe Disease Treatment (Online Pharmacies) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 29: Global: Pompe Disease Treatment (Other Distribution Channels) Market: Sales Value (in Million US$), 2018 & 2023
Figure 30: Global: Pompe Disease Treatment (Other Distribution Channels) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 31: Global: Pompe Disease Treatment (Infantile-Onset Pompe Disease (IOPD)) Market: Sales Value (in Million US$), 2018 & 2023
Figure 32: Global: Pompe Disease Treatment (Infantile-Onset Pompe Disease (IOPD)) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 33: Global: Pompe Disease Treatment (Classic Infantile Form) Market: Sales Value (in Million US$), 2018 & 2023
Figure 34: Global: Pompe Disease Treatment (Classic Infantile Form) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 35: Global: Pompe Disease Treatment (Non-Classic Infantile Form) Market: Sales Value (in Million US$), 2018 & 2023
Figure 36: Global: Pompe Disease Treatment (Non-Classic Infantile Form) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 37: Global: Pompe Disease Treatment (Late-Onset Pompe Disease (LOPD)) Market: Sales Value (in Million US$), 2018 & 2023
Figure 38: Global: Pompe Disease Treatment (Late-Onset Pompe Disease (LOPD)) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 39: Global: Pompe Disease Treatment (Other Indication Types) Market: Sales Value (in Million US$), 2018 & 2023
Figure 40: Global: Pompe Disease Treatment (Other Indication Types) Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 41: North America: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 42: North America: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 43: United States: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 44: United States: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 45: Canada: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 46: Canada: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 47: Asia-Pacific: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 48: Asia-Pacific: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 49: China: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 50: China: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 51: Japan: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 52: Japan: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 53: India: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 54: India: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 55: South Korea: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 56: South Korea: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 57: Australia: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 58: Australia: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 59: Indonesia: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 60: Indonesia: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 61: Others: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 62: Others: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 63: Europe: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 64: Europe: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 65: Germany: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 66: Germany: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 67: France: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 68: France: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 69: United Kingdom: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 70: United Kingdom: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 71: Italy: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 72: Italy: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 73: Spain: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 74: Spain: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 75: Russia: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 76: Russia: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 77: Others: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 78: Others: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 79: Latin America: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 80: Latin America: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 81: Brazil: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 82: Brazil: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 83: Mexico: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 84: Mexico: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 85: Others: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 86: Others: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 87: Middle East and Africa: Pompe Disease Treatment Market: Sales Value (in Million US$), 2018 & 2023
Figure 88: Middle East and Africa: Pompe Disease Treatment Market: Breakup by Country (in %), 2023
Figure 89: Middle East and Africa: Pompe Disease Treatment Market Forecast: Sales Value (in Million US$), 2024-2032
Figure 90: Global: Pompe Disease Treatment Industry: Drivers, Restraints, and Opportunities
Figure 91: Global: Pompe Disease Treatment Industry: Value Chain Analysis
Figure 92: Global: Pompe Disease Treatment Industry: Porter's Five Forces Analysis
List of Tables
Table 1: Global: Pompe Disease Treatment Market: Key Industry Highlights, 2023 & 2032
Table 2: Global: Pompe Disease Treatment Market Forecast: Breakup by Treatment (in Million US$), 2024-2032
Table 3: Global: Pompe Disease Treatment Market Forecast: Breakup by Route of Administration (in Million US$), 2024-2032
Table 4: Global: Pompe Disease Treatment Market Forecast: Breakup by Distribution Channel (in Million US$), 2024-2032
Table 5: Global: Pompe Disease Treatment Market Forecast: Breakup by Indication Type (in Million US$), 2024-2032
Table 6: Global: Pompe Disease Treatment Market Forecast: Breakup by Region (in Million US$), 2024-2032
Table 7: Global: Pompe Disease Treatment Market: Competitive Structure
Table 8: Global: Pompe Disease Treatment Market: Key Players
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