Acquired Orphan Blood Diseases Therapeutics Market Report by Therapy (Recombinant Factor, Immunoglobulin Infusion Therapy, Activated Prothrombin Complex Concentrate, Thrombopoietin Receptor Agonists, and Others), Disease Indication (Acquired Agranulocytosis, Acquired Hemophilia, Acquired Von Willebrand Syndrome, Paroxysmal Nocturnal Hemoglobinuria (PNH), Myelodysplastic Syndrome, and Others), Distribution Channel (Hospital Pharmacy, Retail Pharmacy, and Others), and Region 2025-2033

Acquired Orphan Blood Diseases Therapeutics Market Report by Therapy (Recombinant Factor, Immunoglobulin Infusion Therapy, Activated Prothrombin Complex Concentrate, Thrombopoietin Receptor Agonists, and Others), Disease Indication (Acquired Agranulocytosis, Acquired Hemophilia, Acquired Von Willebrand Syndrome, Paroxysmal Nocturnal Hemoglobinuria (PNH), Myelodysplastic Syndrome, and Others), Distribution Channel (Hospital Pharmacy, Retail Pharmacy, and Others), and Region 2025-2033

Report Format: PDF+Excel | Report ID: SR112025A8217

1   Preface
2   Scope and Methodology

    2.1    Objectives of the Study
    2.2    Stakeholders
    2.3    Data Sources
        2.3.1    Primary Sources
        2.3.2    Secondary Sources
    2.4    Market Estimation
        2.4.1    Bottom-Up Approach
        2.4.2    Top-Down Approach
    2.5    Forecasting Methodology
3   Executive Summary
4   Introduction

    4.1    Overview
    4.2    Key Industry Trends
5   Global Acquired Orphan Blood Diseases Therapeutics Market
    5.1    Market Overview
    5.2    Market Performance
    5.3    Impact of COVID-19
    5.4    Market Forecast
6   Market Breakup by Therapy
    6.1    Recombinant Factor
        6.1.1 Market Trends
        6.1.2 Market Forecast
    6.2    Immunoglobulin Infusion Therapy
        6.2.1 Market Trends
        6.2.2 Market Forecast
    6.3    Activated Prothrombin Complex Concentrate
        6.3.1 Market Trends
        6.3.2 Market Forecast
    6.4    Thrombopoietin Receptor Agonists
        6.4.1 Market Trends
        6.4.2 Market Forecast
    6.5    Others
        6.5.1 Market Trends
        6.5.2 Market Forecast
7   Market Breakup by Disease Indication
    7.1    Acquired Agranulocytosis
        7.1.1 Market Trends
        7.1.2 Market Forecast
    7.2    Acquired Hemophilia
        7.2.1 Market Trends
        7.2.2 Market Forecast
    7.3    Acquired Von Willebrand Syndrome
        7.3.1 Market Trends
        7.3.2 Market Forecast
    7.4    Paroxysmal Nocturnal Hemoglobinuria (PNH)
        7.4.1 Market Trends
        7.4.2 Market Forecast
    7.5    Myelodysplastic Syndrome
        7.5.1 Market Trends
        7.5.2 Market Forecast
    7.6    Others
        7.6.1 Market Trends
        7.6.2 Market Forecast
8   Market Breakup by Distribution Channel
    8.1    Hospital Pharmacy
        8.1.1 Market Trends
        8.1.2 Market Forecast
    8.2    Retail Pharmacy
        8.2.1 Market Trends
        8.2.2 Market Forecast
    8.3    Others
        8.3.1 Market Trends
        8.3.2 Market Forecast
9   Market Breakup by Region
    9.1    North America
        9.1.1 United States
           9.1.1.1 Market Trends
           9.1.1.2 Market Forecast
        9.1.2 Canada
           9.1.2.1 Market Trends
           9.1.2.2 Market Forecast
    9.2    Asia-Pacific
        9.2.1 China
           9.2.1.1 Market Trends
           9.2.1.2 Market Forecast
        9.2.2 Japan
           9.2.2.1 Market Trends
           9.2.2.2 Market Forecast
        9.2.3 India
           9.2.3.1 Market Trends
           9.2.3.2 Market Forecast
        9.2.4 South Korea
           9.2.4.1 Market Trends
           9.2.4.2 Market Forecast
        9.2.5 Australia
           9.2.5.1 Market Trends
           9.2.5.2 Market Forecast
        9.2.6 Indonesia
           9.2.6.1 Market Trends
           9.2.6.2 Market Forecast
        9.2.7 Others
           9.2.7.1 Market Trends
           9.2.7.2 Market Forecast
    9.3    Europe
        9.3.1 Germany
           9.3.1.1 Market Trends
           9.3.1.2 Market Forecast
        9.3.2 France
           9.3.2.1 Market Trends
           9.3.2.2 Market Forecast
        9.3.3 United Kingdom
           9.3.3.1 Market Trends
           9.3.3.2 Market Forecast
        9.3.4 Italy
           9.3.4.1 Market Trends
           9.3.4.2 Market Forecast
        9.3.5 Spain
           9.3.5.1 Market Trends
           9.3.5.2 Market Forecast
        9.3.6 Russia
           9.3.6.1 Market Trends
           9.3.6.2 Market Forecast
        9.3.7 Others
           9.3.7.1 Market Trends
           9.3.7.2 Market Forecast
    9.4    Latin America
        9.4.1 Brazil
           9.4.1.1 Market Trends
           9.4.1.2 Market Forecast
        9.4.2 Mexico
           9.4.2.1 Market Trends
           9.4.2.2 Market Forecast
        9.4.3 Others
           9.4.3.1 Market Trends
           9.4.3.2 Market Forecast
    9.5    Middle East and Africa
        9.5.1 Market Trends
        9.5.2 Market Breakup by Country
        9.5.3 Market Forecast
10  Drivers, Restraints, and Opportunities
    10.1    Overview
    10.2    Drivers
    10.3    Restraints
    10.4    Opportunities
11  Value Chain Analysis
12  Porters Five Forces Analysis

    12.1    Overview
    12.2    Bargaining Power of Buyers
    12.3    Bargaining Power of Suppliers
    12.4    Degree of Competition
    12.5    Threat of New Entrants
    12.6    Threat of Substitutes
13  Price Analysis
14  Competitive Landscape

    14.1    Market Structure
    14.2    Key Players
    14.3    Profiles of Key Players
        14.3.1    Alexion Pharmaceuticals Inc. (AstraZeneca plc)
           14.3.1.1 Company Overview
           14.3.1.2 Product Portfolio
        14.3.2    Amgen Inc.
           14.3.2.1 Company Overview
           14.3.2.2 Product Portfolio
           14.3.2.3 Financials
           14.3.2.4 SWOT Analysis
        14.3.3    GSK plc
           14.3.3.1 Company Overview
           14.3.3.2 Product Portfolio
           14.3.3.3 Financials
           14.3.3.4 SWOT Analysis
        14.3.4    Novartis AG
           14.3.4.1 Company Overview
           14.3.4.2 Product Portfolio
           14.3.4.3 Financials
           14.3.4.4 SWOT Analysis
        14.3.5    Novo Nordisk A/S
           14.3.5.1 Company Overview
           14.3.5.2 Product Portfolio
           14.3.5.3 Financials
           14.3.5.4 SWOT Analysis
        14.3.6    Otsuka Pharmaceutical Co. Ltd.
           14.3.6.1 Company Overview
           14.3.6.2 Product Portfolio
        14.3.7    Rigel Pharmaceuticals Inc.
           14.3.7.1 Company Overview
           14.3.7.2 Product Portfolio
           14.3.7.3 Financials
           14.3.7.4 SWOT Analysis
        14.3.8    Roche Holding AG
           14.3.8.1 Company Overview
           14.3.8.2 Product Portfolio
           14.3.8.3 Financials
        14.3.9    Sanofi 
           14.3.9.1 Company Overview
           14.3.9.2 Product Portfolio
           14.3.9.3 Financials
           14.3.9.4 SWOT Analysis
        14.3.10    Takeda Pharmaceutical Company Limited
           14.3.10.1 Company Overview
           14.3.10.2 Product Portfolio
           14.3.10.3 Financials
           14.3.10.4 SWOT Analysis

Kindly note that this only represents a partial list of companies, and the complete list has been provided in the report.

List of Figures

​Figure 1: Global: Acquired Orphan Blood Diseases Therapeutics Market: Major Drivers and Challenges
Figure 2: Global: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Billion USD), 2019-2024
Figure 3: Global: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Billion USD), 2025-2033
Figure 4: Global: Acquired Orphan Blood Diseases Therapeutics Market: Breakup by Therapy (in %), 2024
Figure 5: Global: Acquired Orphan Blood Diseases Therapeutics Market: Breakup by Disease Indication (in %), 2024
Figure 6: Global: Acquired Orphan Blood Diseases Therapeutics Market: Breakup by Distribution Channel (in %), 2024
Figure 7: Global: Acquired Orphan Blood Diseases Therapeutics Market: Breakup by Region (in %), 2024
Figure 8: Global: Acquired Orphan Blood Diseases Therapeutics (Recombinant Factor) Market: Sales Value (in Million USD), 2019 & 2024
Figure 9: Global: Acquired Orphan Blood Diseases Therapeutics (Recombinant Factor) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 10: Global: Acquired Orphan Blood Diseases Therapeutics (Immunoglobulin Infusion Therapy) Market: Sales Value (in Million USD), 2019 & 2024
Figure 11: Global: Acquired Orphan Blood Diseases Therapeutics (Immunoglobulin Infusion Therapy) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 12: Global: Acquired Orphan Blood Diseases Therapeutics (Activated Prothrombin Complex Concentrate) Market: Sales Value (in Million USD), 2019 & 2024
Figure 13: Global: Acquired Orphan Blood Diseases Therapeutics (Activated Prothrombin Complex Concentrate) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 14: Global: Acquired Orphan Blood Diseases Therapeutics (Thrombopoietin Receptor Agonists) Market: Sales Value (in Million USD), 2019 & 2024
Figure 15: Global: Acquired Orphan Blood Diseases Therapeutics (Thrombopoietin Receptor Agonists) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 16: Global: Acquired Orphan Blood Diseases Therapeutics (Other Therapies) Market: Sales Value (in Million USD), 2019 & 2024
Figure 17: Global: Acquired Orphan Blood Diseases Therapeutics (Other Therapies) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 18: Global: Acquired Orphan Blood Diseases Therapeutics (Acquired Agranulocytosis) Market: Sales Value (in Million USD), 2019 & 2024
Figure 19: Global: Acquired Orphan Blood Diseases Therapeutics (Acquired Agranulocytosis) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 20: Global: Acquired Orphan Blood Diseases Therapeutics (Acquired Hemophilia) Market: Sales Value (in Million USD), 2019 & 2024
Figure 21: Global: Acquired Orphan Blood Diseases Therapeutics (Acquired Hemophilia) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 22: Global: Acquired Orphan Blood Diseases Therapeutics (Acquired Von Willebrand Syndrome) Market: Sales Value (in Million USD), 2019 & 2024
Figure 23: Global: Acquired Orphan Blood Diseases Therapeutics (Acquired Von Willebrand Syndrome) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 24: Global: Acquired Orphan Blood Diseases Therapeutics (Paroxysmal Nocturnal Hemoglobinuria (PNH)) Market: Sales Value (in Million USD), 2019 & 2024
Figure 25: Global: Acquired Orphan Blood Diseases Therapeutics (Paroxysmal Nocturnal Hemoglobinuria (PNH)) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 26: Global: Acquired Orphan Blood Diseases Therapeutics (Myelodysplastic Syndrome) Market: Sales Value (in Million USD), 2019 & 2024
Figure 27: Global: Acquired Orphan Blood Diseases Therapeutics (Myelodysplastic Syndrome) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 28: Global: Acquired Orphan Blood Diseases Therapeutics (Other Disease Indications) Market: Sales Value (in Million USD), 2019 & 2024
Figure 29: Global: Acquired Orphan Blood Diseases Therapeutics (Other Disease Indications) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 30: Global: Acquired Orphan Blood Diseases Therapeutics (Hospital Pharmacy) Market: Sales Value (in Million USD), 2019 & 2024
Figure 31: Global: Acquired Orphan Blood Diseases Therapeutics (Hospital Pharmacy) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 32: Global: Acquired Orphan Blood Diseases Therapeutics (Retail Pharmacy) Market: Sales Value (in Million USD), 2019 & 2024
Figure 33: Global: Acquired Orphan Blood Diseases Therapeutics (Retail Pharmacy) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 34: Global: Acquired Orphan Blood Diseases Therapeutics (Other Distribution Channels) Market: Sales Value (in Million USD), 2019 & 2024
Figure 35: Global: Acquired Orphan Blood Diseases Therapeutics (Other Distribution Channels) Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 36: North America: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 37: North America: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 38: United States: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 39: United States: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 40: Canada: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 41: Canada: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 42: Asia-Pacific: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 43: Asia-Pacific: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 44: China: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 45: China: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 46: Japan: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 47: Japan: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 48: India: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 49: India: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 50: South Korea: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 51: South Korea: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 52: Australia: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 53: Australia: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 54: Indonesia: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 55: Indonesia: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 56: Others: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 57: Others: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 58: Europe: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 59: Europe: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 60: Germany: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 61: Germany: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 62: France: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 63: France: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 64: United Kingdom: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 65: United Kingdom: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 66: Italy: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 67: Italy: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 68: Spain: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 69: Spain: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 70: Russia: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 71: Russia: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 72: Others: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 73: Others: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 74: Latin America: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 75: Latin America: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 76: Brazil: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 77: Brazil: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 78: Mexico: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 79: Mexico: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 80: Others: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 81: Others: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 82: Middle East and Africa: Acquired Orphan Blood Diseases Therapeutics Market: Sales Value (in Million USD), 2019 & 2024
Figure 83: Middle East and Africa: Acquired Orphan Blood Diseases Therapeutics Market: Breakup by Country (in %), 2024
Figure 84: Middle East and Africa: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Sales Value (in Million USD), 2025-2033
Figure 85: Global: Acquired Orphan Blood Diseases Therapeutics Industry: Drivers, Restraints, and Opportunities
Figure 86: Global: Acquired Orphan Blood Diseases Therapeutics Industry: Value Chain Analysis
Figure 87: Global: Acquired Orphan Blood Diseases Therapeutics Industry: Porter's Five Forces Analysis

List of Tables

Table 1: Global: Acquired Orphan Blood Diseases Therapeutics Market: Key Industry Highlights, 2024 & 2033
Table 2: Global: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Breakup by Therapy (in Million USD), 2025-2033
Table 3: Global: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Breakup by Disease Indication (in Million USD), 2025-2033
Table 4: Global: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Breakup by Distribution Channel (in Million USD), 2025-2033
Table 5: Global: Acquired Orphan Blood Diseases Therapeutics Market Forecast: Breakup by Region (in Million USD), 2025-2033
Table 6: Global: Acquired Orphan Blood Diseases Therapeutics Market: Competitive Structure

Acquired Orphan Blood Diseases Therapeutics Market Report by Therapy (Recombinant Factor, Immunoglobulin Infusion Therapy, Activated Prothrombin Complex Concentrate, Thrombopoietin Receptor Agonists, and Others), Disease Indication (Acquired Agranulocytosis, Acquired Hemophilia, Acquired Von Willebrand Syndrome, Paroxysmal Nocturnal Hemoglobinuria (PNH), Myelodysplastic Syndrome, and Others), Distribution Channel (Hospital Pharmacy, Retail Pharmacy, and Others), and Region 2025-2033
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